AAV-mediated liver-directed gene therapy for gyrate atrophy of the choroid and retina
This research will examine some safety issues of liver-directed gene therapy.
Natural History Study of Gyrate Atrophy
The goal of the Gyrate Atrophy Ocular and Systemic Study is to understand the impact of OAT mutations on plasma ornithine levels and retinal degeneration.
Gene Therapy Approach with Liver Hepatocytes
The Wilmer Eye Institute and Department of Genetics, Johns Hopkins University is researching gene therapy to slow or reverse the progression of gyrate atrophy.
Drs. J. Bennett and K. Uyhazi | University of Pennsylvania
Developing gene therapy to slow or reverse the progression of gyrate atrophy